Nobody thinks about epilepsy as a rare disease. But epilepsy syndromes actually make up a large portion of CNS rare diseases. And while progress has been made in developing therapies that treat the symptoms of epilepsy, the true underlying causes can be difficult to pinpoint and treat.
But progress is being made, and Nermina Nakas, MD, MPH and Jane Williams, MD, MPH, Executive Medical Directors in CNS at Syneos Health – and contributors to the book Rare Disease Drug Development: Clinical, Scientific, Patient and Caregiver Perspectives – join Jeff Stewart to discuss recent developments in rare disease epilepsy clinical trials, what they have learned and what drug developers need to know about treating young patients with neurological rare diseases.
For more on the topics covered in this episode, be sure to check out:
Innovation Perspectives in Rare Disease Drug Development
The Syneos Health Podcast: Navigating the Rare Disease Landscape
The Syneos Health Podcast: Mental Health in Rare Disease
Rare Disease Drug Development: Clinical, Scientific, Patient, and Caregiver Perspectives
